Duchenne Muscular Dystrophy (DMD) Global Market & Pipeline

- Approved treatments for DMD and their chemical structures

- Reported net product sales of approved products in DMD from Q3 2014 up to present with forecasts

- Global pipeline of drugs in development for DMD, including disease-modifying treatments, gene therapies, and discontinued/failed drugs (100+ listings). Listed for each drug candidate (where available) is its mechanisms of action, route of administration and dosage, proposed indication, phase or stage of development, key clinical trial identifier, date of clinical trial initiation, no. of trial participants, trial locations (countries & number of sites), the primary outcomes of the trial, trial status and additional notes related to the program and company.

- Global market data (prevalence of DMD, exon data)

- Highlight of SRP-9001/Elevidys key data (summary/notes)

- Brief overview of DMD

Data as of Aug 6 2023.

Delivered as a Microsoft Excel .xlsx document.